Mendelian randomization to inform a clinical trial of chitotriosidase inhibition for pulmonary sarcoidosis

Daniel A. Culver, Marco F. Schmidt, Marlies S. Wijsenbeek-Lourens, Michael Kreuter, Vincent Cottin, Jolanta Kunikowska, Natalia V. Rivera, Marcel Veltkamp, Hannes A. Baukmann, Justin L. Cope, Charles N. J. Ravarani, Zbigniew Zasłona, Theodoros Charitos, Piotr S. Iwanowski
medRxiv 2025.09.25.25336344; doi: https://doi.org/10.1101/2025.09.25.25336344
Preprint
Sep 27, 2025